TY - JOUR A1 - Aballéa, Samuel A1 - Thokagevistk, Katia A1 - Velikanova, Rimma A1 - Simoens, Steven A1 - Annemans, Lieven A1 - Antonanzas, Fernando A1 - Auquier, Pascal A1 - François, Clément A1 - Fricke, Frank-Ulrich A1 - Malone, Daniel A1 - Millier, Aurélie A1 - Persson, Ulf A1 - Petrou, Stavros A1 - Dabbous, Omar A1 - Postma, Maarten A1 - Toumi, Mondher T1 - Health economic evaluation of gene replacement therapies: methodological issues and recommendations JF - Journal of Market Access & Health Policy KW - Gene replacement therapy; guidelines; health economic evaluation; methods; cost- effectiveness analysis; QALY Y1 - 2020 U6 - https://doi.org/10.1080/20016689.2020.1822666 SN - 2001-6689 VL - 8 IS - 1 SP - 2 EP - 16 PB - MDPI AG ER -